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FINDING A CURE
The mission of the Foundation is to fund, promote, and support medical research dedicated to developing treatments and a cure for ML4.
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Your donations directly support ML4 researchers at Harvard, Einstein, Baylor and other top academic institutions dedicated to finding treatments for Mucolipidosis Type IV.
The Latest News
The ML4 Foundation is funding several projects in gene therapy. One of these projects involves a collaboration between Dr. Steven Walkley (Einstein) and Dr. Charles Venditti (NIH). Read here about…
Terrific enrollment by ML4 families in our CoRDS patient registry! In 2015, the ML4 Foundation launched our disease-specific patient registry with Sanford CoRDS. This registry contains clinical records by…
The ML4 Foundation Board of Directors is pleased to report continued funding to: Dr. Yulia Grishchuk (Massachusetts General Hospital) for her proposal, Targeting Neuroinflammation to Treat Mucolipidosis Type IV Dr. Tony…
Read about the exciting progress at Perlara.com in their efforts to screen for compounds to improve MLIV disease. “From Dead to Alive” certainly got our attention! https://www.perlara.com/blog/high-throughput-screen-mliv-flies/