Newly Funded Research

By August 11, 2015 Uncategorized No Comments

The ML4 Foundation Board of Directors is pleased to report approval of funding for Dr. Christian Grimm (University of Munich) for his proposal, Known and novel members of the endolysosomal transportome/channelome as candidates to rescue loss of TRPML1 function in MLIV patients, and to Dr. Diego Medina (TIGEM) for his proposal, High content imaging approaches to investigate TRPML1 modulation and identify compounds inducing clearance in Mucolipidosis type IV.

We are also eagerly anticipating results from recently funded research by Dr. Kirill Kiselyov (University of Pittsburgh), GDAP1 inhibitors as a treatment option for Mucolipidosis Type IV

Each of these projects focusses on treatment options for ML4 patients.

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